Henning Zelba1*, Christina Kyzirakos1, Simone Kayser1, Borong Shao1, Annekathrin Reinhardt1, Natalia Pieper1, Armin Rabsteyn1, Dennis Döcker1,†, Sorin Armeanu-Ebinger2, Matthias Kloor3,Dirk Hadaschik4, Martin Schulze1, Florian Battke5, Alexander Golf6, Saskia Biskup1,4,6
Abstract
Ovarian cancer is one of the most common cancers among women and the most lethal malignancy of all gynecological cancers. Surgery is promising in the early stages; however, most patients are first diagnosed in the advanced stages, where treatment options are limited. Here, we present a 49-year-old patient who was first diagnosed with stage III ovarian cancer. After the tumor progressed several times under guideline therapies with no more treatment options available at that time, the patient received a fully individualized neoantigen-derived peptide vaccine in the setting of an individual healing attempt. The tumor was analyzed for somatic mutations via whole exome sequencing and potential neoepitopes were vaccinated over a period of 50 months. During vaccination, the patient additionally received anti-PD-1 therapy to prevent further disease progression. Vaccine-induced T-cell responses were detected using intracellular cytokine staining. After eleven days of in vitro expansion, four T-cell activation markers (namely IFN-ɣ, TNF-α, IL-2, and CD154) were measured. The proliferation capacity of neoantigen-specific T-cells was determined using a CFSE proliferation assay. Immune monitoring revealed a very strong CD4+ T-cell response against one of the vaccinated peptides. The vaccine-induced T-cells simultaneously expressed CD154, TNF, IL-2, and IFN-ɣ and showed a strong proliferation capacity upon neoantigen stimulation. Next-generation sequencing, as well as immunohistochemical analysis, revealed a loss of Beta-2 microglobulin (B2M), which is essential for MHC class I presentation. The results presented here implicate that the application of neoantigen-derived peptide vaccines might be considered for those cancer stages, where promising therapeutic options are lacking. Furthermore, we provide more data that endorse the intensive investigation of B2M loss as a tumor escape mechanism in clinical trials using anti-cancer vaccines together with immune-checkpoint inhibitors.
1 Zentrum für Humangenetik Tübingen, 72076 Tübingen, Germany
2 Institut für Medizinische Genetik und Angewandte Genomik, Universitätsklinikum Tübingen, 72076 Tübingen, Germany
3 Institut für Pathologie, Heidelberg University Hospital, 69120 Heidelberg, Germany
4 CeCaVa GmbH & Co. KG, 72076 Tübingen, Germany
5 CeGaT GmbH, 72076 Tübingen, Germany
6 MVZ Zentrum für ambulante Onkologie GmbH, 72076 Tübingen, Germany
*Author to whom correspondence should be addressed.
†Formerly at Zentrum für Humangenetik Tübingen, 72076 Tübingen, Germany.